Ronald Cohn

Molecular Genetics


SickKids - Peter Gilgan Centre for Research and Learning
525 University Ave., Suite 960, Toronto, Ontario Canada M5G 2L3
Research Interests
CRISPR-Cas9 and genome engineering, Disease models, Genome analysis and sequencing, Rare diseases

Our research focus spans from gene discoveries to the development of personalized therapies for rare inherited diseases. There are more than 7000 rare diseases worldwide, where children make up 50% of the affected population. Among all the rare diseases, only 5% have treatments. We are part of the effort in developing therapies mediated through gene editing and gene modulation strategies for these hereditary rare diseases.